Dong Hyun Jo, Hyewon Jang, Chang Sik Cho, Seok Jae Lee, Ji Hwa Heo, Jung Ah Kim, Se Jin Kim, WonHyoung Ryu, Chan-Wook Park, Byeong-Cheol Kang, Heon Yung Gee, Young Hoon Sung*, Hyongbum Henry Kim*, and Jeong Hun Kim*
Intravitreal adenine base editing of RS1 improves vision in a preclinical mouse model of retinoschisis
Molecular Therapy
Date: Apr 18, 2025